Achieving the Promise of Gene Therapy: New Pathways to Overcome Patient Enrollment, operational and Safety Challenges
02월 10일 (목)
10:00-11:00
Rare Disease Recruitment: Addressing enrollment hurdles and differentiating your clinical trial in an increasingly competitive research environment
02월 10일 (목)
11:00-12:00
Natural History vs. Registry Studies in Rare Disease: Which, When, and How?
02월 10일 (목)
12:00-13:00
Lunch
02월 10일 (목)
13:00-14:00
How to Navigate Global Regulatory Frameworks for Gene Therapy Development and how to develop a successful clinical trial strategy considering diverse local regulatory frameworks.